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CLINICAL_TRIALS research · 2026-03-27

Clinical Trial Update: A Study of Sepiapterin in Participants With Phenylketonuria (PKU) [Phase 3]

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Summary

Phase 3 clinical trial investigating sepiapterin for phenylketonuria is currently recruiting participants.

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Diseases / indications

Drugs mentioned

  • Sepiapterin (sepiapterin)

Snippet

Sponsor: PTC Therapeutics | Conditions: Phenylketonuria | Phase 3 | Status: RECRUITING