Clinical Trial Update: Gene Therapy With Modified Autologous Hematopoietic Stem Cells for Patients With Mucopolysaccharidosis Type II [Phase 1, Phase 2]

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Summary

This clinical trial update describes a gene therapy using modified autologous hematopoietic stem cells for Mucopolysaccharidosis type II, currently in Phase 1/2…

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Diseases / indications

• Mucopolysaccharidosis Type Ii

Drugs mentioned

• Autologous hematopoietic stem cell gene therapy for Mucopolysaccharidosis type II

Snippet

Sponsor: University of Manchester | Conditions: Mucopolysaccharidosis II | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING