Clinical Trial Update: Efficacy METAZYM for the Treatment Metachromatic Leukodystrophy Treated With Hematopoietic Stem Cell Transplantation [Phase 2]

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Summary

This Phase 2 trial update reports on the efficacy of METAZYM for metachromatic leukodystrophy in patients who received hematopoietic stem cell transplantation.

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Diseases / indications

• Metachromatic Leukodystrophy

Drugs mentioned

• METAZYM

Snippet

Sponsor: Assistance Publique - Hôpitaux de Paris | Conditions: Metachromatic Leukodystrophy | Phase 2 | Status: COMPLETED