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CLINICAL_TRIALS research · 2026-03-30

Clinical Trial Update: A Study to Provide Continued Access to Mitapivat for Participants Who Previously Completed an Agios-Sponsored Mitapivat Study [Phase 4]

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Summary

This document outlines a Phase 4 study providing continued access to mitapivat for participants who previously completed an Agios-sponsored mitapivat trial.

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Diseases / indications

Drugs mentioned

  • Pyrukynd (mitapivat)

Snippet

Sponsor: Agios Pharmaceuticals, Inc. | Conditions: Pyruvate Kinase Deficiency, Anemia, Hemolytic | Phase 4 | Status: ENROLLING_BY_INVITATION