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CLINICAL_TRIALS research · 2026-04-01

Clinical Trial Update: Phase 1/2 Clinical Trial of PR001 in Infants With Type 2 Gaucher Disease (PROVIDE) [Phase 1, Phase 2]

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Summary

Phase 1/2 clinical trial update for PR001 in infants with Gaucher disease type 2 (PROVIDE), currently active and not recruiting.

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Diseases / indications

Drugs mentioned

  • PR001

Snippet

Sponsor: Prevail Therapeutics | Conditions: Gaucher Disease, Type 2 | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING