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CLINICAL_TRIALS trial_result · 2026-04-02

Clinical Trial Update: Study Assessing Long-term Safety and Efficacy of Alpelisib in Patients With PIK3CA-Related Overgrowth Spectrum (PROS) Who Previously Participated in Study CBYL719F12002 (EPIK-P1) [Phase 2]

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Summary

This clinical trial update describes a Phase 2 long-term safety and efficacy study of alpelisib in patients with PIK3CA-related overgrowth spectrum (PROS) who p…

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Diseases / indications

Drugs mentioned

  • Alpelisib (alpelisib)

Snippet

Sponsor: Novartis Pharmaceuticals | Conditions: PIK3CA-related Overgrowth Spectrum (PROS) | Phase 2 | Status: ACTIVE_NOT_RECRUITING