Clinical Trial Update: A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy [Phase 4]

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Summary

A Phase 4 clinical trial is evaluating whether risdiplam provides effective and safe benefits when given as an early intervention after gene therapy in pediatri…

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Diseases / indications

• Spinal Muscular Atrophy

Drugs mentioned

• EVRYSDI (risdiplam)

Snippet

Sponsor: Hoffmann-La Roche | Conditions: Muscular Atrophy, Spinal | Phase 4 | Status: RECRUITING