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CLINICAL_TRIALS research · 2026-04-03

Clinical Trial Update: A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C [Phase 3]

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Summary

A pivotal Phase 3 trial evaluating N-Acetyl-L-Leucine for Niemann-Pick disease type C is currently recruiting.

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Diseases / indications

Drugs mentioned

  • N-Acetyl-L-Leucine (N-acetyl-L-leucine)

Snippet

Sponsor: IntraBio Inc | Conditions: Niemann-Pick Disease, Type C | Phase 3 | Status: RECRUITING