Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2026-04-07

Clinical Trial Update: Expanded Access to Mepsevii

View source ↗

Summary

Expanded access program for Mepsevii (vestronidase alfa) for patients with mucopolysaccharidosis VII is currently available.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • Mepsevii (vestronidase alfa)

Snippet

Sponsor: Ultragenyx Pharmaceutical Inc | Conditions: MPS VII, Mucopolysaccharidosis VII | Status: AVAILABLE