CLINICAL_TRIALS
trial_result
· 2026-04-07
Clinical Trial Update: Expanded Access to Mepsevii
Summary
Expanded access program for Mepsevii (vestronidase alfa) for patients with mucopolysaccharidosis VII is currently available.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Ultragenyx Pharmaceutical Inc | Conditions: MPS VII, Mucopolysaccharidosis VII | Status: AVAILABLE