Clinical Trial Update: Registry of Patients Diagnosed With Lysosomal Storage Diseases

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Summary

This ClinicalTrials.gov registry entry describes ongoing recruitment for a registry of patients diagnosed with various lysosomal storage diseases, including sev…

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Diseases / indications

• Gaucher Disease Neuronopathic
• Mucopolysaccharidosis Type
• Mucopolysaccharidosis Type Ii
• Mucopolysaccharidosis Type Iv
• Mucopolysaccharidosis Type Vi
• Mucopolysaccharidosis Type Vii
• Pompe Disease Infantile-onset
• Wolman Disease

Snippet

Sponsor: University of California, San Francisco | Conditions: Mucopolysaccharidosis I, Mucopolysaccharidosis II | Status: RECRUITING