Clinical Trial Update: Observation Study in Patients Age 0-5 Years With LAMA2-related Congenital Muscular Dystrophy

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Summary

An observational study recruiting children aged 0-5 years with LAMA2-related congenital muscular dystrophy (MDC1A) to characterize disease features and natural …

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Diseases / indications

• Merosin-deficient Congenital Muscular Dystrophy Mdc1a

Snippet

Sponsor: Nationwide Children's Hospital | Conditions: LAMA2-MD \(Merosin Deficient Congenital Muscular Dystrophy, MDC1A\) | Status: RECRUITING