Clinical Trial Update: Longitudinal Assessment of Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency Patients

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Summary

An update on a longitudinal assessment study of patients with Tripeptidyl peptidase 1 enzyme deficiency, including CLN2 disease and related neuronal ceroid lipo…

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Diseases / indications

• Neuronal Ceroid Lipofuscinoses
• Neuronal Ceroid Lipofuscinosis Cln2
• Spinocerebellar Ataxia Type

Snippet

Sponsor: Children's Hospital of Orange County | Conditions: Neuronal Ceroid-Lipofuscinoses, Neuronal Ceroid Lipofuscinosis CLN2 | Status: ACTIVE_NOT_RECRUITING