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CLINICAL_TRIALS research · 2026-04-08

Clinical Trial Update: Clinical and Laboratory Study of Methylmalonic Acidemia

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Summary

This entry reports an ongoing clinical and laboratory study of methylmalonic acidemia, a metabolic disorder, sponsored by the National Human Genome Research Ins…

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Diseases / indications

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Sponsor: National Human Genome Research Institute (NHGRI) | Conditions: Organic Acidemia, Methylmalonic Acidemia | Status: RECRUITING