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CLINICAL_TRIALS research · 2026-04-09

Clinical Trial Update: Observational Study to Characterize Biomarkers and Disease Progression in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome

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Summary

An observational trial to characterize biomarkers and disease progression in MECP2 duplication syndrome sponsored by Ionis Pharmaceuticals has been terminated.

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Diseases / indications

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Sponsor: Ionis Pharmaceuticals, Inc. | Conditions: Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome | Status: TERMINATED