Clinical Trial Update: AAV2/8-LSPhGAA (ACTUS-101) in Late-Onset Pompe Disease [Phase 1]

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Summary

Phase 1 clinical trial ACTUS-101 (AAV2/8-LSPhGAA) for late-onset Pompe disease has completed.

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Diseases / indications

• Pompe Disease

Drugs mentioned

• AAV2/8-LSPhGAA (ACTUS-101)

Snippet

Sponsor: AskBio Inc | Conditions: Pompe Disease | Phase 1 | Status: COMPLETED