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CLINICAL_TRIALS trial_result · 2026-04-13

Clinical Trial Update: MAD of IVT VP-001 in PRPF31 Mutation-Associated Retinal Dystrophy Subjects (Wallaby) [Phase 1]

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Summary

Phase 1 Wallaby trial evaluating intravitreal VP-001 in PRPF31 mutation–associated retinal dystrophy has completed the dose-ranging maximum tolerated dose asses…

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Diseases / indications

Drugs mentioned

  • VP-001

Snippet

Sponsor: PYC Therapeutics | Conditions: Retinitis Pigmentosa 11, Retinal Degeneration | Phase 1 | Status: COMPLETED