CLINICAL_TRIALS
trial_result
· 2026-04-13
Clinical Trial Update: MAD of IVT VP-001 in PRPF31 Mutation-Associated Retinal Dystrophy Subjects (Wallaby) [Phase 1]
Summary
Phase 1 Wallaby trial evaluating intravitreal VP-001 in PRPF31 mutation–associated retinal dystrophy has completed the dose-ranging maximum tolerated dose asses…
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: PYC Therapeutics | Conditions: Retinitis Pigmentosa 11, Retinal Degeneration | Phase 1 | Status: COMPLETED