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CLINICAL_TRIALS research · 2026-04-13

Clinical Trial Update: Natural History of PRPF31 Mutation-Associated Retinal Dystrophy

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Summary

This clinical trial update describes an ongoing natural history study of PRPF31 mutation-associated retinal dystrophy, an inherited retinal condition that can p…

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Diseases / indications

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Sponsor: PYC Therapeutics | Conditions: Retinitis Pigmentosa, Eye Diseases, Hereditary | Status: ACTIVE_NOT_RECRUITING