Clinical Trial Update: A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy [Phase 4]

View source ↗

Summary

A Phase 4 trial is evaluating the effectiveness and safety of risdiplam in pediatric spinal muscular atrophy patients who experienced a plateau or decline after…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Spinal Muscular Atrophy

Drugs mentioned

• Risdiplam (risdiplam)

Snippet

Sponsor: Hoffmann-La Roche | Conditions: Muscular Atrophy, Spinal | Phase 4 | Status: RECRUITING