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CLINICAL_TRIALS research · 2026-04-14

Clinical Trial Update: Lysosomal Acid Lipase Deficiency in Risk Groups

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Summary

AstraZeneca is recruiting participants for a clinical trial addressing lysosomal acid lipase deficiency in at-risk groups.

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Diseases / indications

Drugs mentioned

  • KANUMA (Sebelipase alfa)

Snippet

Sponsor: AstraZeneca | Conditions: Lysosomal Acid Lipase Deficiency | Status: RECRUITING