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CLINICAL_TRIALS research · 2026-04-14

Clinical Trial Update: A Phase 1b/2a, Open-label Single Ascending Doses and Multiple Ascending Doses Study in Participants With Pi*ZZ AATD [Phase 1, Phase 2]

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Summary

Phase 1b/2a open-label study in adults with Pi*ZZ Alpha-1 Antitrypsin Deficiency is active/not recruiting, sponsored by Wave Life Sciences.

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Diseases / indications

Snippet

Sponsor: Wave Life Sciences Ltd. | Conditions: Alpha-1 Antitrypsin Deficiency | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING