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CLINICAL_TRIALS research · 2026-04-15

Clinical Trial Update: Low-Dose Sirolimus to Increase Hematopoietic Function in Patients With RUNX1 Familial Platelet Disorder [Phase 2]

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Summary

A Phase 2 clinical trial update describes evaluating low-dose sirolimus to improve hematopoietic function in patients with familial platelet disorder caused by …

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Diseases / indications

Drugs mentioned

  • Sirolimus (Sirolimus)

Snippet

Sponsor: M.D. Anderson Cancer Center | Conditions: Familial Platelet Disorder, Hematopoietic | Phase 2 | Status: RECRUITING