CLINICAL_TRIALS
research
· 2026-04-15
Clinical Trial Update: ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia [Phase 1, Phase 2]
Summary
A Phase 1/2 clinical trial of ALS20-101, a lentiviral gene therapy for beta-thalassemia, is currently recruiting.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Children's Hospital of Philadelphia | Conditions: Beta-Thalassemia | Phase 1, Phase 2 | Status: RECRUITING