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CLINICAL_TRIALS research · 2026-04-15

Clinical Trial Update: ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia [Phase 1, Phase 2]

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Summary

A Phase 1/2 clinical trial of ALS20-101, a lentiviral gene therapy for beta-thalassemia, is currently recruiting.

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Diseases / indications

Drugs mentioned

  • ALS20-101 Lentiviral Gene Therapy

Snippet

Sponsor: Children's Hospital of Philadelphia | Conditions: Beta-Thalassemia | Phase 1, Phase 2 | Status: RECRUITING