Clinical Trial Update: Safety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency [Phase 1, Phase 2]

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Summary

This clinical trial update concerns the safety and potential efficacy of GS-100 Gene Therapy for NGLY1 Deficiency in Phase 1/2 and indicates the study is curren…

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Diseases / indications

• Ngly1 Deficiency

Drugs mentioned

• GS-100 Gene Therapy

Snippet

Sponsor: Grace Science, LLC | Conditions: NGLY1 Deficiency | Phase 1, Phase 2 | Status: RECRUITING