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CLINICAL_TRIALS ClinicalTrials.gov record update

Safety and Efficacy of AAV9/AP4B1 For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47): A Phase 1/2 Single-Center, Open-Label Study of Stereotactic Intra-cisterna Magna Administration

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Record identity and dates

Source
ClinicalTrials.gov
Source record ID
NCT06948019
Title field or adapter rule
protocolSection.identificationModule.officialTitle
Ingested At
2026-04-25T22:27:52.002673+00:00
Published At
2025-04-28T00:00:00+00:00
Record Updated At
2025-04-28
Timestamp Basis
source retrieval time was not retained by the feed adapter
Date limitation
source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions
["HSP", "Hereditary Spastic Paraplegia", "Hereditary Spastic Paraparesis", "Hereditary Spastic Paraplegia Type 50", "Hereditary Spastic Paraplegia Type 47", "Hereditary Spastic Paraplegia Type 51", "Hereditary Spastic Paraplegia Type 52", "SPG47", "AP4B1", "Neurogenetic Disorders", "Neurodevelopmental Conditions", "Movement Disorders", "Gene Therapy"]
protocolSection.statusModule.lastUpdatePostDateStruct.date
"2025-04-28"
protocolSection.identificationModule.nctId
"NCT06948019"
protocolSection.identificationModule.officialTitle
"Safety and Efficacy of AAV9/AP4B1 For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47): A Phase 1/2 Single-Center, Open-Label Study of Stereotactic Intra-cisterna Magna Administration"
protocolSection.statusModule.overallStatus
"NOT_YET_RECRUITING"
protocolSection.designModule.phases
["PHASE1", "PHASE2"]
protocolSection.statusModule.resultsFirstPostDateStruct.date
""

Study condition terms

  • HSP (protocolSection.conditionsModule.conditions)
  • Hereditary Spastic Paraplegia (protocolSection.conditionsModule.conditions)
  • Hereditary Spastic Paraparesis (protocolSection.conditionsModule.conditions)
  • Hereditary Spastic Paraplegia Type 50 (protocolSection.conditionsModule.conditions)
  • Hereditary Spastic Paraplegia Type 47 (protocolSection.conditionsModule.conditions)
  • Hereditary Spastic Paraplegia Type 51 (protocolSection.conditionsModule.conditions)
  • Hereditary Spastic Paraplegia Type 52 (protocolSection.conditionsModule.conditions)
  • SPG47 (protocolSection.conditionsModule.conditions)
  • AP4B1 (protocolSection.conditionsModule.conditions)
  • Neurogenetic Disorders (protocolSection.conditionsModule.conditions)
  • Neurodevelopmental Conditions (protocolSection.conditionsModule.conditions)
  • Movement Disorders (protocolSection.conditionsModule.conditions)
  • Gene Therapy (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

This index keeps the source fields it imported; it may not contain the complete original record. Verify wording and context in the linked source.