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CLINICAL_TRIALS trial_result · 2023-07-24

Clinical Trial Update: Danicopan as Add-on Therapy to a C5 Inhibitor in Paroxysmal Nocturnal Hemoglobinuria (PNH) Participants Who Have Clinically Evident Extravascular Hemolysis (EVH)(ALPHA) [Phase 3]

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Summary

This Phase 3 study evaluates danicopan as an add-on therapy to a C5 inhibitor in Paroxysmal Nocturnal Hemoglobinuria patients with extravascular hemolysis; the …

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Diseases / indications

Drugs mentioned

  • Danicopan (danicopan)

Snippet

Sponsor: Alexion Pharmaceuticals, Inc. | Conditions: Paroxysmal Nocturnal Hemoglobinuria | Phase 3 | Status: COMPLETED | Results posted: 2023-07-24