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CLINICAL_TRIALS research · 2025-05-06

Clinical Trial Update: A Study to Learn About the Effect of Higher Doses of Nusinersen (BIIB058) Given as Injections to Participants With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Risdiplam (ASCEND) [Phase 3]

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Summary

An ongoing Phase 3 clinical trial is evaluating higher doses of nusinersen (BIIB058) given by injections in SMA patients who previously received risdiplam, to a…

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Diseases / indications

Drugs mentioned

  • Nusinersen (nusinersen)
  • Risdiplam (risdiplam)

Snippet

Sponsor: Biogen | Conditions: Spinal Muscular Atrophy | Phase 3 | Status: ACTIVE_NOT_RECRUITING