Clinical Trial Update: A Prospective Study to Observe & Describe Clinical Outcomes of Alglucosidase Alfa Treatment in Patients ≤6 Months of Age With Infantile-onset Pompe Disease (IOPD)

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Summary

This clinical trial update describes a prospective study to observe clinical outcomes of alglucosidase alfa treatment in infants ≤6 months with infantile-onset …

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Diseases / indications

• Pompe Disease

Drugs mentioned

• LUMIZYME (ALGLUCOSIDASE ALFA)

Snippet

Sponsor: Sanofi | Conditions: Glycogen Storage Disease Type II | Status: ACTIVE_NOT_RECRUITING