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CLINICAL_TRIALS research · 2025-05-14

Clinical Trial Update: Administration of MELPIDA to Determine the Safety and Efficacy for Patients With Spastic Paraplegia Type 50 [Phase 1]

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Summary

A Phase 1 clinical trial evaluating the safety and potential efficacy of MELPIDA in patients with hereditary spastic paraplegia (Spastic Paraplegia Type 50) is …

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Diseases / indications

Drugs mentioned

  • Melpida (AAV9-hAP4M1opt gene therapy)

Snippet

Sponsor: The Hospital for Sick Children | Conditions: Spastic Paraplegia Type 50 | Phase 1 | Status: ACTIVE_NOT_RECRUITING