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CLINICAL_TRIALS research · 2025-05-14

Clinical Trial Update: A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

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Summary

This clinical trial update notes that a real-world effectiveness study of pegcetacoplan for Paroxysmal nocturnal hemoglobinuria is currently recruiting.

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Diseases / indications

Drugs mentioned

  • Pegcetacoplan (Pegcetacoplan)

Snippet

Sponsor: Swedish Orphan Biovitrum | Conditions: Paroxysmal Nocturnal Hemoglobinuria | Status: RECRUITING