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CLINICAL_TRIALS trial_result · 2025-05-15

Clinical Trial Update: Post-authorization Safety Study of Iptacopan in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) Using Data From the IPIG PNH Registry

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Summary

Post-authorization safety study evaluating iptacopan in adults with paroxysmal nocturnal hemoglobinuria using data from the IPIG PNH registry.

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Diseases / indications

Drugs mentioned

  • iptacopan (iptacopan)

Snippet

Sponsor: Novartis Pharmaceuticals | Conditions: Hemoglobinuria, Paroxysmal | Status: ACTIVE_NOT_RECRUITING