Clinical Trial Update: Study of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Participants With GM1 Gangliosidosis [Phase 1, Phase 2]

View source ↗

Summary

Gemma Biotherapeutics reports an ongoing Phase 1/2 trial evaluating PBGM01 for safety, tolerability, and efficacy in pediatric GM1 gangliosidosis (types I and I…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Gm1 Gangliosidosis
• Gm1 Gangliosidosis Type
• Gm1 Gangliosidosis Type Ii

Drugs mentioned

• PBGM01

Snippet

Sponsor: Gemma Biotherapeutics | Conditions: GM1 Gangliosidosis, GM1 Gangliosidosis, Type I | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING