Clinical Trial Update: GBE Deficiency (GSD IV and APBD) Natural History Study

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Summary

Observational natural history study of GBE deficiency including Glycogen Storage Disease Type IV and Adult Polyglucosan Body Disease, currently recruiting.

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Diseases / indications

• Glycogen Storage Disease Type Iv
• Polyglucosan Body Disease

Snippet

Sponsor: Duke University | Conditions: Glycogen Storage Disease Type IV, Adult Polyglucosan Body Disease | Status: RECRUITING