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CLINICAL_TRIALS trial_result · 2025-05-30

Clinical Trial Update: Long Term Beta Thalassemia Treatment: Findings From The Extension Period [Phase 2]

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Summary

Long-term extension-period findings from a Phase 2 trial evaluating treatment for beta-thalassemia are reported.

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Diseases / indications

Snippet

Sponsor: National Institute of Blood and Marrow Transplant (NIBMT), Pakistan | Conditions: Fetal Hemoglobin, Beta-Thalassemia | Phase 2 | Status: ACTIVE_NOT_RECRUITING