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CLINICAL_TRIALS research · 2025-06-11

Clinical Trial Update: A Study of Pegcetacoplan in Pediatric Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) [Phase 2]

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Summary

A Phase 2 clinical trial update indicates that pegcetacoplan for pediatric patients with paroxysmal nocturnal hemoglobinuria is currently recruiting.

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Diseases / indications

Drugs mentioned

  • Pegcetacoplan (Pegcetacoplan)

Snippet

Sponsor: Apellis Pharmaceuticals, Inc. | Conditions: Paroxysmal Nocturnal Hemoglobinuria (PNH), Paroxysmal Hemoglobinuria | Phase 2 | Status: RECRUITING