Clinical Trial Update: Intravitreal ERT to Prevent Retinal Disease Progression in Children With CLN2 [Phase 1, Phase 2]

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Summary

A Phase 1/2 clinical trial evaluating intravitreal enzyme replacement therapy to prevent retinal disease progression in children with Neuronal Ceroid Lipofuscin…

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Diseases / indications

• Neuronal Ceroid Lipofuscinosis Type

Drugs mentioned

• Intravitreal enzyme replacement therapy (ERT)

Snippet

Sponsor: David L Rogers, MD | Conditions: Neuronal Ceroid Lipofuscinosis Type 2 | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING