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CLINICAL_TRIALS research · 2025-06-15

Clinical Trial Update: Ivacaftor Impact in an Adolescent Without a Cystic Fibrosis-Associated CFTR (Cystic Fibrosis Transmembrane Conductance Regulator) Mutation for Chronic Pancreatitis: Single-Patient Study Tracking Flare Frequency and Health Data Compared to Historical Records.

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Summary

A single-patient study investigates whether ivacaftor affects flare frequency and health data in an adolescent with chronic pancreatitis who does not have a CFT…

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Diseases / indications

Drugs mentioned

  • Ivacaftor (Kalydeco) (ivacaftor)

Snippet

Sponsor: Mission: Cure | Conditions: Chronic Pancreatitis | Status: ACTIVE_NOT_RECRUITING