Clinical Trial Update: Evaluation of the Safety and Efficacy of Late-onset Pompe Disease Gene Therapy Drug [Phase 1, Phase 2]

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Summary

This clinical trial update describes an investigational gene therapy for late-onset Pompe disease being evaluated in Phase 1/2, currently recruiting.

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Diseases / indications

• Pompe Disease

Drugs mentioned

• Pompe disease gene therapy (late-onset) — investigational

Snippet

Sponsor: GeneCradle Inc | Conditions: Pompe Disease (Late-onset) | Phase 1, Phase 2 | Status: RECRUITING