CLINICAL_TRIALS
research
· 2025-07-03
Clinical Trial Update: Physician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry Disease
Summary
A physician-initiated expanded access request for migalastat in individual Fabry disease patients is being tracked, with the program listed as available.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Amicus Therapeutics | Conditions: Fabry Disease | Status: AVAILABLE