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CLINICAL_TRIALS research · 2025-07-03

Clinical Trial Update: Physician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry Disease

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Summary

A physician-initiated expanded access request for migalastat in individual Fabry disease patients is being tracked, with the program listed as available.

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Diseases / indications

Drugs mentioned

  • Migalastat (migalastat)

Snippet

Sponsor: Amicus Therapeutics | Conditions: Fabry Disease | Status: AVAILABLE