Clinical Trial Update: Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 1 Patients [Phase 1, Phase 2]

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Summary

A clinical trial update indicates a gene therapy drug is being evaluated for safety and efficacy in Spinal Muscular Atrophy Type 1, currently recruiting in Phas…

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Diseases / indications

• Spinal Muscular Atrophy

Drugs mentioned

• Gene therapy drug

Snippet

Sponsor: GeneCradle Inc | Conditions: Spinal Muscular Atrophy | Phase 1, Phase 2 | Status: RECRUITING