Clinical Trial Update: Evaluation of the Safety and Efficacy of Infantile-onset Pompe Disease Gene Therapy Drug [Phase 1, Phase 2]

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Summary

This clinical trial update describes a Phase 1/2 evaluation of a gene therapy for infantile-onset Pompe disease, with the study currently active but not recruit…

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Diseases / indications

• Pompe Disease

Drugs mentioned

• Infantile-onset Pompe disease gene therapy

Snippet

Sponsor: GeneCradle Inc | Conditions: Pompe Disease Infantile-Onset | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING