Clinical Trial Update: Study of Sodium Phenylbutyrate (ACER-001) for the Treatment of Pediatric and Adults Patients With Medium Chain Acyl-CoA Dehydrogenase Deficiency (MCADD) [Phase 2]

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Summary

A Phase 2 trial evaluating ACER-001 (sodium phenylbutyrate) for treatment of Medium-chain Acyl-CoA Dehydrogenase Deficiency in pediatric and adult patients is c…

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Diseases / indications

• Medium-chain Acyl-coa Dehydrogenase Deficiency

Drugs mentioned

• ACER-001 (sodium phenylbutyrate)

Snippet

Sponsor: Jerry Vockley, MD, PhD | Conditions: Medium-chain Acyl-CoA Dehydrogenase Deficiency | Phase 2 | Status: RECRUITING