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CLINICAL_TRIALS research · 2025-07-14

Clinical Trial Update: Safety, Tolerability, and Efficacy Study of Valoctocogene Roxaparvovec in Hemophilia A With Active or Prior Inhibitors [Phase 1, Phase 2]

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Summary

This clinical trial update describes safety, tolerability, and efficacy data for valoctocogene roxaparvovec in Hemophilia A patients with inhibitors, evaluated …

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Diseases / indications

Drugs mentioned

  • Roctavian (valoctocogene roxaparvovec)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Hemophilia A With Inhibitor, Hemophilia A With Anti Factor VIII | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING