CLINICAL_TRIALS
research
· 2025-07-14
Clinical Trial Update: Safety, Tolerability, and Efficacy Study of Valoctocogene Roxaparvovec in Hemophilia A With Active or Prior Inhibitors [Phase 1, Phase 2]
Summary
This clinical trial update describes safety, tolerability, and efficacy data for valoctocogene roxaparvovec in Hemophilia A patients with inhibitors, evaluated …
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Snippet
Sponsor: BioMarin Pharmaceutical | Conditions: Hemophilia A With Inhibitor, Hemophilia A With Anti Factor VIII | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING