Tuberous Sclerosis Complex
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2026-03-18Clinical Trial Update: Remote Assessment and Intervention for Behavior Problems in Kids With TSC [NA]
A UCLA-led clinical trial examining remote assessment and intervention for behavior problems in children with tuberous sclerosis complex has…
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CLINICAL_TRIALS trial_result · 2026-01-21Clinical Trial Update: Feasibility of [11C]Acetate-PET in LAM and TSC [Phase 1, Phase 2]
Phase 1/2 feasibility study evaluating [11C]Acetate-PET imaging in lymphangioleiomyomatosis and tuberous sclerosis complex. Results have bee…
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CLINICAL_TRIALS trial_result · 2026-01-09Clinical Trial Update: Precision Medicine for Neurocutaneous Syndromes in Western China
A completed clinical trial from West China Hospital exploring precision medicine approaches for neurocutaneous syndromes, including NF1, TSC…
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CLINICAL_TRIALS trial_result · 2025-12-01Clinical Trial Update: Topical Sirolimus Ointment for Cutaneous Angiofibromas in Subjects With Tuberous Sclerosis Complex [Phase 2]
Phase 2 trial evaluating topical sirolimus ointment for cutaneous angiofibromas in tuberous sclerosis complex subjects was terminated; resul…
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CLINICAL_TRIALS trial_result · 2025-11-21Clinical Trial Update: Study to Evaluate the Pharmacokinetics and Safety Effects Following Coadministration of Carbamazepine or Itraconazole With Radiprodil in Healthy Adults [Phase 1]
Phase 1 study evaluating pharmacokinetics and safety of coadministering Radiprodil with Carbamazepine or Itraconazole in healthy adults; the…
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CLINICAL_TRIALS trial_result · 2025-10-31Clinical Trial Update: Assessment of Adjunctive Cannabidiol Oral Solution (GWP42003-P) in Children With Tuberous Sclerosis Complex (TSC), Dravet Syndrome (DS), or Lennox-Gastaut Syndrome (LGS) Who Experience Inadequately-controlled Seizures [Phase 3]
A Phase 3 study of adjunctive cannabidiol oral solution GWP42003-P in children with tuberous sclerosis complex, Dravet syndrome, or Lennox-G…
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CLINICAL_TRIALS trial_result · 2025-10-01Clinical Trial Update: Open-label Study of Adjunctive GNX Treatment in Children and Adults With TSC-related Epilepsy [Phase 3]
Open-label Phase 3 trial of adjunctive ganaxolone (GNX) for Tuberous Sclerosis Complex–related epilepsy in children and adults was terminate…
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CLINICAL_TRIALS trial_result · 2025-07-11Clinical Trial Update: Adjunctive GNX Treatment Compared With Placebo in Children and Adults With TSC-related Epilepsy [Phase 3]
A Phase 3 study evaluating adjunctive ganaxolone (GNX) versus placebo for tuberous sclerosis complex-related epilepsy has completed and resu…
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CLINICAL_TRIALS trial_result · 2025-06-04Clinical Trial Update: Basimglurant (NOE-101) in Children, Adolescents, and Young Adults With TSC [Phase 2]
A Phase 2 study of Basimglurant (NOE-101) in children, adolescents, and young adults with tuberous sclerosis complex has completed.
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CLINICAL_TRIALS trial_result · 2025-01-23Clinical Trial Update: Predicting Epileptogenic Tubers in Patients with Tuberous Sclerosis Complex
A completed clinical trial from Beijing Children's Hospital investigated predicting epileptogenic tubers in patients with tuberous sclerosis…
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CLINICAL_TRIALS trial_result · 2025-01-17Clinical Trial Update: The Effectiveness and Safety of Resective Epilepsy Surgery for TRE
This clinical trial update reports on the effectiveness and safety of resective epilepsy surgery for tuberous sclerosis complex–related epil…
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CLINICAL_TRIALS trial_result · 2024-12-19Clinical Trial Update: The Effectiveness and Safety of Vagus Nerve Stimulation for TRE
A completed clinical trial evaluated the effectiveness and safety of vagus nerve stimulation for tuberous sclerosis complex–associated epile…
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CLINICAL_TRIALS trial_result · 2024-11-22Clinical Trial Update: Clinical Study of NPC-12Y Gel in Patients With Skin Lesions Associated With TSC [Phase 3]
Phase 3 clinical trial evaluating NPC-12Y Gel for skin lesions in Tuberous Sclerosis Complex has completed.
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CLINICAL_TRIALS trial_result · 2024-11-06Clinical Trial Update: KidneYou - Innovative Digital Therapy [NA]
Completed clinical trial update for KidneYou, an innovative digital therapy from Advice Pharma Group srl, investigating use in chronic kidne…
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CLINICAL_TRIALS trial_result · 2024-10-30Clinical Trial Update: TSC Remote Assessment and Intervention [NA]
Clinical trial update for Tuberous sclerosis complex remote assessment and intervention (NCT04698538) indicates the study is completed.
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CLINICAL_TRIALS trial_result · 2024-08-19Clinical Trial Update: Preventing Epilepsy Using Vigabatrin In Infants With Tuberous Sclerosis Complex [Phase 2]
A Phase 2 trial evaluated whether vigabatrin can prevent epilepsy in infants with tuberous sclerosis complex; the study results were posted …
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CLINICAL_TRIALS trial_result · 2024-05-16Clinical Trial Update: Stopping TSC Onset and Progression 2: Epilepsy Prevention in TSC Infants [Phase 1, Phase 2]
This entry reports the completion of the Phase 1/2 trial Stopping TSC Onset and Progression 2, which studied epilepsy prevention in infants …
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CLINICAL_TRIALS trial_result · 2024-02-08Clinical Trial Update: Efficacy and Safety of Rapamycin Versus Vigabatrin in the Prevention of Tuberous Sclerosis Complex Symptoms in Infants [Phase 2, Phase 3]
A clinical trial comparing rapamycin to vigabatrin for prevention of Tuberous Sclerosis Complex symptoms in infants, spanning Phase 2 and Ph…
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CLINICAL_TRIALS trial_result · 2023-08-08Clinical Trial Update: Placebo Controlled Study to Assess the Efficacy and Safety of Rapamycin in Drug Resistant Epilepsy Associated With Tuberous Sclerosis Complex [Phase 3]
A Phase 3 placebo-controlled trial evaluating rapamycin for drug-resistant epilepsy in tuberous sclerosis complex is recruiting.
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CLINICAL_TRIALS trial_result · 2022-07-14Clinical Trial Update: An Open-label Extension Trial of Cannabidiol (GWP42003-P, CBD) for Seizures in Tuberous Sclerosis Complex (GWPCARE6) [Phase 3]
Open-label extension of cannabidiol (GWP42003-P) in seizures associated with tuberous sclerosis complex completed Phase 3.
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CLINICAL_TRIALS trial_result · 2022-04-25Clinical Trial Update: RAPAMYCIN FOR KIDNEY ANGIOMYOLIPOMAS [Phase 2]
Phase 2 trial update for rapamycin targeting kidney angiomyolipomas associated with tuberous sclerosis; trial completed with results posted.
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CLINICAL_TRIALS trial_result · 2021-09-09Clinical Trial Update: Safety and Efficacy of Everolimus (Afinitor®) in Chinese Adult Patients With Angiomyolipoma Associated With Tuberous Sclerosis Complex. [Phase 4]
Phase 4 trial assessing safety and efficacy of Everolimus (Afinitor) in Chinese adults with angiomyolipoma associated with tuberous sclerosi…
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CLINICAL_TRIALS trial_result · 2021-09-01Clinical Trial Update: A Pilot Study To Evaluate The Effects of Everolimus on Brain mTOR Activity and Cortical Hyperexcitability in TSC and FCD [Phase 2]
Phase 2 pilot study evaluating everolimus on brain mTOR activity and cortical hyperexcitability in epilepsy related to tuberous sclerosis co…
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CLINICAL_TRIALS trial_result · 2021-03-29Clinical Trial Update: Rapalogues for Autism Phenotype in TSC: A Feasibility Study [Phase 2]
Phase 2 feasibility study evaluating rapalogue treatment for autism phenotype in tuberous sclerosis complex with self-injury; study complete…
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CLINICAL_TRIALS trial_result · 2020-09-23Clinical Trial Update: A Randomized Controlled Trial of Cannabidiol (GWP42003-P, CBD) for Seizures in Tuberous Sclerosis Complex (GWPCARE6) [Phase 3]
Phase 3 randomized trial assessing cannabidiol (GWP42003-P CBD) for seizures in tuberous sclerosis complex has completed with results posted…