Transthyretin Amyloidosis
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CLINICAL_TRIALS research · 2024-12-09Clinical Trial Update: Prevalence and Prediction of ATTR in Ambulatory Patients With HFpEF [NA]
A Massachusetts General Hospital study is recruiting to assess how common transthyretin amyloidosis is and how to predict its presence in am…
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CLINICAL_TRIALS research · 2024-12-03Clinical Trial Update: PL_GNT01_ISR_Grant 53234273
A clinical trial update indicates that the PL_GNT01_ISR_Grant study (NCT06714019) is currently enrolling by invitation for transthyretin-rel…
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CLINICAL_TRIALS trial_result · 2024-11-22Clinical Trial Update: Transthyretin Amyloidosis Outcome Survey (THAOS)
Pfizer-sponsored THAOS transthyretin amyloidosis registry study has completed and posted results.
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CLINICAL_TRIALS research · 2024-10-23Clinical Trial Update: Prevalence and Significance of ATTR Aortic Valve Amyloidosis in Degenerative Aortic Stenosis [NA]
This trial investigates the prevalence and clinical significance of transthyretin (ATTR) amyloidosis of the aortic valve in patients with de…
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CLINICAL_TRIALS trial_result · 2024-06-11Clinical Trial Update: Positron Emission Tomography / Magnetic Resonance Imaging in Aortic Stenosis
An update on a completed clinical trial evaluating the use of PET/MRI imaging in patients with Aortic stenosis and Transthyretin amyloidosis…
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CLINICAL_TRIALS trial_result · 2023-12-06Clinical Trial Update: The Study of an Investigational Drug, Patisiran (ALN-TTR02), for the Treatment of Transthyretin (TTR)-Mediated Amyloidosis in Participants Who Have Already Been Treated With ALN-TTR02 (Patisiran) [Phase 3]
Phase 3 trial update for patisiran in patients with transthyretin-mediated amyloidosis who have already been treated with patisiran; study c…
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CLINICAL_TRIALS trial_result · 2023-02-09Clinical Trial Update: Extension Study Assessing Long Term Safety and Efficacy of IONIS-TTR Rx in Familial Amyloid Polyneuropathy (FAP) [Phase 3]
An extensionPhase 3 trial evaluated long-term safety and efficacy of IONIS-TTR Rx in familial amyloid polyneuropathy, with completed status …
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CLINICAL_TRIALS trial_result · 2022-08-11Clinical Trial Update: HELIOS-A: A Study of Vutrisiran (ALN-TTRSC02) in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis) [Phase 3]
HELIOS-A, a Phase 3 study of vutrisiran (ALN-TTRSC02) in patients with hereditary transthyretin amyloidosis (hATTR) has completed and posted…
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CLINICAL_TRIALS trial_result · 2021-12-21Clinical Trial Update: Patisiran in Patients With Hereditary Transthyretin-mediated Amyloidosis (hATTR Amyloidosis) Disease Progression Post-Liver Transplant [Phase 3]
Phase 3 trial evaluating patisiran in hereditary transthyretin-mediated amyloidosis patients with disease progression after liver transplant…
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CLINICAL_TRIALS trial_result · 2021-07-15Clinical Trial Update: The Effect of Tafamidis on Transthyretin Stabilization, Safety, Tolerability and Efficacy in Transthyretin Amyloid Polyneuropathy Patients [Phase 4]
A Phase 4 clinical trial update evaluating tafamidis for transthyretin amyloidosis, focusing on stabilization, safety, tolerability, and eff…
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FDA approval · 2021-06-01FDA Approved: VYNDAMAX — Supplemental Application (Pfizer Laboratories Div Pfizer Inc)
FDA approved a supplemental application for VYNDAMAX (tafamidis) submitted by Pfizer Laboratories Div Pfizer Inc.
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CLINICAL_TRIALS trial_result · 2016-05-12Clinical Trial Update: Safety and Efficacy Study of Doxycycline/UrsoDeoxyCholicAcid on Disease Progression in ATTR Amyloidosis [Phase 2]
A Phase 2 safety and efficacy trial evaluating doxycycline with ursodeoxycholic acid in transthyretin amyloidosis with cardiomyopathy has co…
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CLINICAL_TRIALS trial_result · 2016-02-25Clinical Trial Update: Safety, Efficacy and Pharmacokinetics of Doxycycline Plus Tauroursodeoxycholic Acid in Transthyretin Amyloidosis [Phase 2]
Phase 2 trial evaluating safety, efficacy and pharmacokinetics of a doxycycline plus tauroursodeoxycholic acid combination in transthyretin …
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CLINICAL_TRIALS trial_result · 2015-08-24Clinical Trial Update: The Effect of Diflunisal on Familial Transthyretin Amyloidosis
Completed clinical trial evaluating the NSAID diflunisal for hereditary transthyretin-mediated amyloidosis (familial transthyretin amyloidos…