Spinal Muscular Atrophy
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2015-07-03Clinical Trial Update: Study to Evaluate Sodium Phenylbutyrate in Pre-symptomatic Infants With Spinal Muscular Atrophy [Phase 1, Phase 2]
This update reports the completion and posted results of a Phase 1/2 clinical trial evaluating sodium phenylbutyrate in pre-symptomatic infa…
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CLINICAL_TRIALS trial_result · 2015-06-15Clinical Trial Update: CARNIVAL Type I: Valproic Acid and Carnitine in Infants With Spinal Muscular Atrophy (SMA) Type I [Phase 1, Phase 2]
This clinical trial update reports on a Phase 1/2 study evaluating valproic acid and carnitine in infants with spinal muscular atrophy, with…
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CLINICAL_TRIALS trial_result · 2015-03-23Clinical Trial Update: Differential Study of Muscle Transcriptome [NA]
This update notes that a clinical trial examining differential muscle transcriptome in amyotrophic lateral sclerosis, spinal muscular atroph…
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CLINICAL_TRIALS trial_result · 2014-03-05Clinical Trial Update: Clinical Assessment of Spinal Muscular Atrophy Type II and III (SMA Europe) [NA]
The SMA Europe-sponsored clinical assessment of Spinal Muscular Atrophy Type II and III, sponsored by Institut de Myologie in France, has co…
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CLINICAL_TRIALS trial_result · 2013-12-18Clinical Trial Update: Pilot Study of Growth Hormon to Treat SMA Typ II and III [Phase 2]
A Phase 2 pilot trial evaluating growth hormone (somatropin) for spinal muscular atrophy type II and III has completed.
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CLINICAL_TRIALS trial_result · 2013-11-13Clinical Trial Update: Optimum Insufflation Capacity in NMD [NA]
This ClinicalTrials.gov update for NCT01981915 indicates completion of a study on optimum insufflation capacity in neuromuscular diseases, i…
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CLINICAL_TRIALS trial_result · 2013-03-12Clinical Trial Update: Progressive Strength Training in Spinal Muscular Atrophy [NA]
Completed clinical trial evaluating progressive strength training in spinal muscular atrophy; results were posted in March 2013.
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CLINICAL_TRIALS trial_result · 2013-02-15Clinical Trial Update: Study to Evaluate the Efficacy of Riluzole in Children and Young Adults With Spinal Muscular Atrophy (SMA) [Phase 2, Phase 3]
A phase 2/3 clinical trial evaluating riluzole for spinal muscular atrophy has completed.
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CLINICAL_TRIALS trial_result · 2012-10-24Clinical Trial Update: A Pilot Study of Biomarkers for Spinal Muscular Atrophy
This update reports the completion of a pilot clinical trial evaluating biomarkers for Spinal Muscular Atrophy.
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CLINICAL_TRIALS trial_result · 2012-01-31Clinical Trial Update: Spinal Muscular Atrophy and Cardiac Autonomic Function [NA]
This entry notes the completion of a clinical trial examining spinal muscular atrophy and cardiac autonomic function.
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CLINICAL_TRIALS trial_result · 2011-05-03Clinical Trial Update: Valproic Acid and Carnitine in Patients With Spinal Muscular Atrophy [Phase 2]
This clinical trial update reports a completed Phase 2 study evaluating valproic acid and L-carnitine in patients with Spinal Muscular Atrop…
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CLINICAL_TRIALS trial_result · 2010-07-20Clinical Trial Update: Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type I [Phase 1, Phase 2]
A Phase 1/2 trial of sodium phenylbutyrate in children with spinal muscular atrophy Type I was terminated, with results posted in 2010.
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CLINICAL_TRIALS trial_result · 2010-02-15Clinical Trial Update: A Trial of Hydroxyurea in Spinal Muscular Atrophy [Phase 2, Phase 3]
Phase 2/Phase 3 trial evaluating hydroxyurea in spinal muscular atrophy has completed.
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CLINICAL_TRIALS trial_result · 2009-12-16Clinical Trial Update: Evaluation of the Muscle Strength and Motor Ability in Children With Spinal Muscle Atrophy(SMA) Treated With Valproic Acid
This completed clinical trial evaluated whether valproic acid can improve muscle strength and motor function in children with spinal muscula…