Spinal Muscular Atrophy
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CLINICAL_TRIALS research · 2024-10-09Clinical Trial Update: Therapeutic Management and Use of Resources and Costs of Spinal Muscular Atrophy in Spain
This completed clinical trial sponsored by Novartis analyzes therapeutic management and the use of resources and costs associated with spina…
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CLINICAL_TRIALS research · 2024-09-24Clinical Trial Update: Ultrasonographic Muscle Assessment and Functional Scales in Spinal Muscular Atrophy
An active-not-recruiting clinical trial from Istanbul University Cerrahpasa is investigating ultrasonographic muscle assessment and function…
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CLINICAL_TRIALS research · 2024-08-20Clinical Trial Update: Hippotherapy in Children With Spinal Muscular Atrophy [NA]
A clinical trial in the Czech Republic is evaluating hippotherapy as an intervention for children with spinal muscular atrophy; the study is…
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CLINICAL_TRIALS research · 2024-08-16Clinical Trial Update: Exploring Bulbar Function, Speech And Communication Development in SMA Type 1
A clinical trial is ongoing to study bulbar function, speech, and communication development in infants with spinal muscular atrophy type 1, …
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CLINICAL_TRIALS research · 2024-08-06Clinical Trial Update: Outcome Measures and Biomarkers in a Cohort of Spinal Muscular Atrophy Type III/ IV Patients [NA]
This is an observational study update examining outcome measures and biomarkers in spinal muscular atrophy type III/IV patients. It is spons…
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CLINICAL_TRIALS research · 2024-07-23Clinical Trial Update: UK SMA Patient Registry
The UK Spinal Muscular Atrophy (SMA) patient registry sponsored by Newcastle University is currently recruiting.
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CLINICAL_TRIALS research · 2019-01-17Clinical Trial Update: Reliability and Validity of the ACTIVE-mini for Quantifying Movement in Infants With Spinal Muscular Atrophy
Clinical trial update examining the reliability and validity of the ACTIVE-mini movement assessment for infants with spinal muscular atrophy…
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CLINICAL_TRIALS research · 2016-11-02Clinical Trial Update: A Study to Collect Blood Samples From Patients With Spinal Muscular Atrophy for Biomarker Analysis
A completed study collected blood samples from patients with spinal muscular atrophy to analyze potential biomarkers.
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CLINICAL_TRIALS research · 2016-08-12Clinical Trial Update: Clinical Trial of Exercise in Patients With Spinal Muscular Atrophy (SMA) [NA]
This entry notes a completed clinical trial evaluating exercise in patients with spinal muscular atrophy. The study was sponsored by Columbi…
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CLINICAL_TRIALS research · 2016-08-04Clinical Trial Update: Allogeneic Adipose Derived Stem Cells for Werdnig Hoffman Patients [Phase 1, Phase 2]
A Phase 1/2 clinical trial at Tehran University of Medical Sciences is evaluating allogeneic adipose-derived stem cells in infants with spin…
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CLINICAL_TRIALS research · 2016-01-01Clinical Trial Update: Valproate and Levocarnitine in Children With Spinal Muscular Atrophy [Phase 3]
Phase 3 clinical trial update evaluating valproate and levocarnitine in children with spinal muscular atrophy.
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CLINICAL_TRIALS research · 2014-04-28Clinical Trial Update: National Registry for Egyptian Pediatric Neuromuscular Diseases
This document provides an update on Egypt's National Registry for Pediatric Neuromuscular Diseases, cataloging Spinal Muscular Atrophy, Musc…