Hereditary Hemorrhagic Telangiectasia
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EMA withdrawal · 2026-08-04EMA Application withdrawn: Orblid (bevacizumab) — Laboratoires Delbert
The EMA has withdrawn the application for Orblid (bevacizumab) by Laboratoires Delbert for hereditary telangiectasia/hemorrhagic conditions.
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CLINICAL_TRIALS trial_result · 2026-06-04Clinical Trial Results: Sirolimus for Nosebleeds in HHT [Phase 2]
Phase 2 clinical trial results for sirolimus in treating nosebleeds associated with hereditary hemorrhagic telangiectasia have been complete…
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CLINICAL_TRIALS trial_result · 2026-04-24Clinical Trial Update: Ultra-low-dose Chest CT for HHT
A Mayo Clinic-sponsored trial evaluating ultra-low-dose chest CT for hereditary hemorrhagic telangiectasia has completed.
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CLINICAL_TRIALS trial_result · 2026-04-22Clinical Trial Update: Cerebral Hemorrhage Risk in Hereditary Hemorrhagic Telangiectasia
The document notes the completion of a clinical trial evaluating cerebral hemorrhage risk in hereditary hemorrhagic telangiectasia, sponsore…
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CLINICAL_TRIALS research · 2026-04-22Clinical Trial Update: CHORUS - Comprehensive HHT Outcomes Registry of the United States (Formerly OUR HHT Registry)
The CHORUS registry (NCT04150822) is an ongoing US outcomes registry for hereditary hemorrhagic telangiectasia (formerly OUR HHT), sponsored…
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CLINICAL_TRIALS withdrawal · 2026-04-13Clinical Trial Update: A Trial of TER-1754 in Patients With Hereditary Hemorrhagic Telangiectasia [Phase 1]
The Phase 1 trial of TER-1754 for hereditary hemorrhagic telangiectasia has been withdrawn.
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CLINICAL_TRIALS research · 2026-04-03Clinical Trial Update: A Study to Evaluate ALN-6400 in Healthy Volunteers and Patients With Hereditary Hemorrhagic Telangiectasia (HHT) [Phase 1, Phase 2]
A clinical trial evaluating ALN-6400 in healthy volunteers and patients with Hereditary Hemorrhagic Telangiectasia is currently recruiting i…
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CLINICAL_TRIALS research · 2026-03-27Clinical Trial Update: Bevacizumab In Hereditary Hemorrhagic Telangiectasia [Phase 2]
A Phase 2 clinical trial of bevacizumab for hereditary hemorrhagic telangiectasia is currently active but not recruiting.
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CLINICAL_TRIALS trial_result · 2026-03-19Clinical Trial Update: Effects of Pazopanib on Hereditary Hemorrhagic Telangiectasia Related Epistaxis and Anemia (Paz) [Phase 2, Phase 3]
This document reports an ongoing Phase 2/Phase 3 clinical trial evaluating pazopanib for hereditary hemorrhagic telangiectasia-related epist…
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CLINICAL_TRIALS research · 2026-03-17Clinical Trial Update: Assess Safety and Efficacy of VAD044 in HHT Patients [Phase 1, Phase 2]
Ongoing Phase 1/2 study evaluating the safety and efficacy of VAD044 for hereditary hemorrhagic telangiectasia (HHT); the trial is currently…
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CLINICAL_TRIALS research · 2026-03-16Clinical Trial Update: Quality of Life in Pediatric Participants With HHT
A clinical trial update describes a planned study to assess quality of life in pediatric participants with hereditary hemorrhagic telangiect…
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CLINICAL_TRIALS research · 2026-03-11Clinical Trial Update: Pregnancy in Women With Rare Multisystemic Vascular Diseases: COGRare5 Study
The document announces the COGRare5 study recruiting pregnant women with rare multisystemic vascular diseases. Diseases under study include …
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CLINICAL_TRIALS research · 2026-03-11Clinical Trial Update: Efficacy of Nintedanib for Treatment of Epistaxis in Hereditary Hemorrhagic Telangiectasia (HHT) Patients [Phase 2]
A Phase 2 clinical trial is evaluating nintedanib for reducing epistaxis in patients with hereditary hemorrhagic telangiectasia and is curre…
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CLINICAL_TRIALS trial_result · 2026-03-03Clinical Trial Update: Efficacy and Tolerance of Treatment With Bevacizumab for Severe Liver Involvement With High Cardiac Output in Hereditary Hemorrhagic Telangiectasia Within the French Hereditary Hemorrhagic Telangiectasia Network
A clinical trial update reports on the efficacy and tolerability of Bevacizumab for severe liver involvement with high cardiac output in her…
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CLINICAL_TRIALS research · 2026-02-17Clinical Trial Update: Non-Invasive Detection of Pulmonary Right-to-Left Shunts Using the SONAS Ultrasound Device [NA]
A recruiting clinical trial evaluating a non-invasive SONAS ultrasound device to detect pulmonary right-to-left shunts in patients with here…
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CLINICAL_TRIALS trial_result · 2025-12-19Clinical Trial Update: Efficacy and Safety of Bevacizumab for the Treatment Hemorrhagic Hereditary Telangiectasia (HHT) Associated With Severe Hepatic Vascular Malformations. Phase II Study [Phase 2]
Phase II trial evaluating bevacizumab for efficacy and safety in hereditary hemorrhagic telangiectasia with severe hepatic vascular malforma…
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CLINICAL_TRIALS trial_result · 2025-12-19Clinical Trial Update: Stress-Echography in Hereditary Haemorrhagic Telangiectasia Patient With Hepatic Involvement [NA]
A clinical trial update notes that a stress-echography study in a patient with hereditary hemorrhagic telangiectasia and hepatic involvement…
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CLINICAL_TRIALS research · 2025-10-03Clinical Trial Update: Immunological Effects of Iron Supplementation in HHT Disease [NA]
A clinical trial in Lyon is investigating the immunological effects of iron supplementation in patients with hereditary hemorrhagic telangie…
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CLINICAL_TRIALS trial_result · 2025-09-25Clinical Trial Update: Description of the Impact of Symptoms on Quality of Life in HHT Disease: DISQUO
A completed DISQUO study update describing how symptoms impact quality of life for people with hereditary hemorrhagic telangiectasia (HHT).
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CLINICAL_TRIALS research · 2025-09-23Clinical Trial Update: Pomalidomide for the Treatment of Bleeding in Hereditary Hemorrhagic Telangiectasia Longitudinal Assessment Study
A clinical trial update indicating pomalidomide is being studied for bleeding in hereditary hemorrhagic telangiectasia in a longitudinal ass…
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CLINICAL_TRIALS trial_result · 2025-09-10Clinical Trial Update: Diagnostic Value of Ultra-low Dose Thoracic Scanner for the Pulmonary Arteriovenous Malformation Detection in HHT Patient [NA]
This completed trial evaluated the diagnostic value of an ultra-low-dose thoracic scanner for detecting pulmonary arteriovenous malformation…
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CLINICAL_TRIALS research · 2025-09-03Clinical Trial Update: Genotype Expression and Phenotype of Endothelial Cells, Carrying an ACVRL1, ENG or SMAD4 Mutation, in Response to BMP9 for the Identification of New Therapeutic Targets in Hereditary Haemorrhagic Telangiectasia [NA]
Clinical trial investigating how endothelial cells with ACVRL1, ENG, or SMAD4 mutations respond to BMP9 to identify new therapeutic targets …
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CLINICAL_TRIALS other · 2025-08-14Clinical Trial Update: Cardiac Evaluation in Hereditary Hemorrhagic Telangiectasia
A clinical trial update describes a planned cardiac evaluation in patients with Hereditary Hemorrhagic Telangiectasia, currently not yet rec…
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CLINICAL_TRIALS trial_result · 2025-08-08Clinical Trial Update: Efficacy of a Timolol Nasal Spray as a Treatment for Epistaxis in Hereditary Hemorrhagic Telangiectasia (HHT) - (TEMPO) [Phase 2]
A Phase 2 trial evaluating timolol nasal spray for epistaxis in hereditary hemorrhagic telangiectasia has completed, reporting on its effica…
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CLINICAL_TRIALS trial_result · 2025-08-06Clinical Trial Update: BABH Study: Efficacy and Safety of Bevacizumab on Severe Bleedings Associated With Hemorrhagic Hereditary Telangiectasia (HHT). [Phase 3]
Phase 3 trial evaluating bevacizumab for efficacy and safety in reducing severe bleeding in hereditary hemorrhagic telangiectasia has comple…