Facioscapulohumeral Muscular Dystrophy
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CLINICAL_TRIALS research · 2025-01-13Clinical Trial Update: Magnetic Resonance Imaging and Ultrasound Comparison With Load Evaluation
A clinical trial update describes a study comparing magnetic resonance imaging and ultrasound with load evaluation in patients with faciosca…
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CLINICAL_TRIALS research · 2024-12-02Clinical Trial Update: Testing a Tailored Home Exercise Program to Reduce Pain and Fatigue in Patients with FSHD. [NA]
Clinical trial update for a tailored home exercise program aimed at reducing pain and fatigue in people with facioscapulohumeral muscular dy…
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CLINICAL_TRIALS research · 2024-07-24Clinical Trial Update: Disease Burden and Living Situation of Patients With Facioscapulohumeral Muscular Dystrophy
This clinical trial update describes a study assessing disease burden and living situations for patients with facioscapulohumeral muscular d…
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CLINICAL_TRIALS research · 2024-05-09Clinical Trial Update: The United Kingdom Facioscapulohumeral Muscular Dystrophy Patient Registry
A UK patient registry for facioscapulohumeral muscular dystrophy is currently recruiting participants to collect observational data.
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CLINICAL_TRIALS research · 2023-08-18Clinical Trial Update: Safety, Tolerability, Pharmacokinetics (PK), and Activity of ATYR1940 in Participants With Muscular Dystrophy - Study Extension [Phase 1, Phase 2]
Clinical trial extension study examining safety, tolerability, pharmacokinetics, and activity of ATYR1940 in participants with facioscapuloh…
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CLINICAL_TRIALS research · 2018-04-12Clinical Trial Update: Rasch-analysis of Clinical Severity in FSHD
This document reports a Rasch-analysis study of clinical severity in Facioscapulohumeral Muscular Dystrophy using data from a completed tria…
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CLINICAL_TRIALS research · 2017-04-27Clinical Trial Update: Intramuscular Transplantation of Muscle Derived Stem Cell and Adipose Derived Mesenchymal Stem Cells in Patients With Facioscapulohumeral Dystrophy (FSHD) [Phase 1]
Phase 1 clinical trial evaluating intramuscular transplantation of muscle-derived stem cells and adipose-derived mesenchymal stem cells in p…