Fabry Disease
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2014-08-22Clinical Trial Update: Extension Study of TKT028 Evaluating Safety and Clinical Outcomes of Replagal® in Adult Patients With Fabry Disease [Phase 3]
Phase 3 extension study update on Replagal in adults with Fabry disease assessing safety and clinical outcomes.
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CLINICAL_TRIALS trial_result · 2014-07-10Clinical Trial Update: A Study Evaluating Glycosphingolipid Clearance in Patients Treated With Agalsidase Alfa Who Switch to Agalsidase Beta [Phase 4]
Phase 4 study evaluating glycosphingolipid clearance in Fabry disease patients who switch from agalsidase alfa to agalsidase beta.
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CLINICAL_TRIALS trial_result · 2014-06-18Clinical Trial Update: A Phase 1 Study To Evaluate the Safety of Migalastat Hydrochloride Given Intravenously to Healthy Volunteers [Phase 1]
A Phase 1 study evaluating the safety of intravenous migalastat hydrochloride in healthy volunteers has completed.
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CLINICAL_TRIALS trial_result · 2014-06-06Clinical Trial Update: Safety and Efficacy Study of Several Replagal Dosing Regimens on Cardiac Function in Adults With Fabry Disease [Phase 3]
Phase 3 trial assessing safety and efficacy of several Replagal dosing regimens on cardiac function in adults with Fabry disease completed w…
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CLINICAL_TRIALS trial_result · 2014-05-28Clinical Trial Update: Pulmonary Involvement in Patients With Fabry Disease
Clinical trial update summarizing a study that investigates pulmonary involvement in Fabry disease, with the study status noted as completed…
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CLINICAL_TRIALS trial_result · 2014-05-20Clinical Trial Update: Safety Study of Replagal® Therapy in Children With Fabry Disease [Phase 2]
Phase 2 safety study of Replagal therapy in children with Fabry disease has completed with results posted in 2014.
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CLINICAL_TRIALS trial_result · 2014-04-25Clinical Trial Update: This Study is Designed to Evaluate PD/PK and Safety of Replagal Manufactured by Two Different Processes. [Phase 2]
Phase 2 clinical trial evaluating pharmacokinetics, pharmacodynamics, and safety of Replagal produced by two manufacturing processes in Fabr…
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CLINICAL_TRIALS trial_result · 2014-03-18Clinical Trial Update: Paricalcitol in Fabry Disease [NA]
Clinical trial update on paricalcitol in Fabry disease; the study status is completed.
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CLINICAL_TRIALS trial_result · 2013-12-18Clinical Trial Update: A Phase I, Randomized, Single-Blind, Four-Period Cross-Over, Placebo-Controlled, Dose-Escalation Study to Evaluate the Safety and Pharmacokinetics of Single Oral Doses of GR181413A/AT1001 in Healthy Japanese Subjects [Phase 1]
A Phase 1, randomized, single-blind, four-period cross-over, placebo-controlled, dose-escalation study in healthy Japanese subjects evaluati…
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CLINICAL_TRIALS trial_result · 2013-12-18Clinical Trial Update: Migalastat Food Effect Study [Phase 1]
Phase 1 study assessing the effect of food on migalastat in Fabry disease has completed. The update reports results from the food-effect tri…
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CLINICAL_TRIALS trial_result · 2013-12-18Clinical Trial Update: A Study to Assess the Absorption, Metabolism and Excretion of Migalastat Hydrochloride (AT1001-014) [Phase 1]
Phase 1 study update assessing how migalastat hydrochloride is absorbed, metabolized, and excreted in Fabry disease. The trial is sponsored …
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CLINICAL_TRIALS trial_result · 2013-12-04Clinical Trial Update: A Study of the Safety and Efficacy of Fabrazyme in Patients With Fabry Disease [Phase 3]
Phase 3 clinical trial update reporting on the safety and efficacy of Fabrazyme for Fabry disease; study completed.
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CLINICAL_TRIALS trial_result · 2013-11-19Clinical Trial Update: The Fabrazyme® and Arbs and ACE Inhibitor Treatment (FAACET) Study
This completed FAACET study evaluated Fabrazyme in combination with ARB/ACE inhibitor therapy in Fabry disease patients with proteinuria. Th…
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CLINICAL_TRIALS trial_result · 2013-11-19Clinical Trial Update: Antiproteinuric Agents and Fabry Disease
This clinical trial update reports a completed study evaluating antiproteinuric agents in Fabry disease with proteinuria.
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CLINICAL_TRIALS trial_result · 2013-10-10Clinical Trial Update: Replagal Enzyme Replacement Therapy for Children With Fabry Disease [Phase 2]
Phase 2 trial update for Replagal enzyme replacement therapy in children with Fabry disease; study completed with results posted in 2013.
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CLINICAL_TRIALS trial_result · 2013-04-04Clinical Trial Update: Prevalence of Fabry's Disease in a Population of Patients With Chronic Pains [NA]
This completed clinical trial evaluated the prevalence of Fabry disease in a population of patients with chronic pain.
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CLINICAL_TRIALS trial_result · 2011-08-17Clinical Trial Update: An Open-Label Maintenance Study of the Enzyme Replacement Therapy Replagal in Patients With Fabry Disease [Phase 1]
An open-label Phase 1 maintenance study of Replagal (agalsidase alfa) for Fabry disease has been completed, according to the trial record.
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CLINICAL_TRIALS trial_result · 2010-12-15Clinical Trial Update: A Study of the Safety and Efficacy of Fabrazyme (Agalsidase Beta) as Compared to Placebo in Patients With Advanced Fabry Disease [Phase 4]
Phase 4 clinical trial comparing Fabrazyme (agalsidase beta) to placebo in patients with advanced Fabry disease completed; results were post…
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CLINICAL_TRIALS trial_result · 2010-08-18Clinical Trial Update: A Study of the Safety and Efficacy of Fabrazyme in Patients With Fabry Disease [Phase 4]
Phase 4 trial evaluating the safety and efficacy of Fabrazyme in patients with Fabry disease; results were posted in 2010.
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CLINICAL_TRIALS trial_result · 2009-12-21Clinical Trial Update: Fabry : National Initiative of Screening [NA]
The document reports completion of a Fabry disease screening trial within ischemic stroke patients under the National Initiative of Screenin…
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CLINICAL_TRIALS trial_result · 2009-06-16Clinical Trial Update: A Study of Fabrazyme in Pediatric Patients With Fabry Disease [Phase 2]
This clinical trial update summarizes Phase 2 results from a pediatric study of Fabrazyme in patients with Fabry disease.
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CLINICAL_TRIALS trial_result · 2009-04-02Clinical Trial Update: A Study of the Safety and Efficacy of Fabrazyme in Patients With Fabry Disease [Phase 2]
Phase 2 study evaluating Fabrazyme for Fabry disease assessed safety and efficacy; results were posted in 2009.
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CLINICAL_TRIALS trial_result · 2009-02-05Clinical Trial Update: Severe Renal Disease Study in Fabry Patients Treated With Fabrazyme [Phase 2]
Phase 2 trial of Fabrazyme in Fabry disease patients with severe renal disease was terminated; results were posted in 2009.
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CLINICAL_TRIALS trial_result · 2008-03-04Clinical Trial Update: Alternative Dosing and Regimen of Replagal to Treat Fabry Disease [Phase 2]
Phase 2 trial evaluating alternative dosing regimens of Replagal (agalsidase alfa) for Fabry disease has been completed.
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CLINICAL_TRIALS trial_result · 2008-03-04Clinical Trial Update: Alpha-Galactosidase A Replacement Therapy for Fabry Disease [Phase 2]
A Phase 2 trial of Alpha-Galactosidase A replacement therapy for Fabry disease has completed.